Amylyx Pharmaceuticals Announces European Commission Grants Orphan Drug Designation For AMX0035 For Wolfram Syndrome; Topline Data From Phase 2 HELIOS Trial Expected Fall 2024.
Portfolio Pulse from Benzinga Newsdesk
Amylyx Pharmaceuticals has received Orphan Drug Designation from the European Commission for its drug AMX0035, aimed at treating Wolfram Syndrome. The company expects topline data from its Phase 2 HELIOS trial in Fall 2024.
August 02, 2024 | 1:01 pm
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Amylyx Pharmaceuticals has been granted Orphan Drug Designation by the European Commission for AMX0035, targeting Wolfram Syndrome. This regulatory milestone could positively impact the stock, with further potential upside when Phase 2 HELIOS trial data is released in Fall 2024.
The Orphan Drug Designation is a significant regulatory milestone that can lead to market exclusivity and other benefits, likely boosting investor sentiment. The anticipation of Phase 2 trial data adds further potential for stock appreciation.
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