Neurogene Says NGN-401 Gene Therapy For Rett Syndrome Has Been Selected To Participate In FDA Support For Clinical Trials Advancing Rare Disease Therapeutics Pilot Program
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Neurogene's NGN-401 gene therapy for Rett Syndrome has been selected for the FDA's START Program, which aims to accelerate the development of rare disease therapeutics. The therapy is currently in a Phase 1/2 clinical trial evaluating two dose levels.
June 03, 2024 | 11:45 am
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Neurogene's NGN-401 gene therapy for Rett Syndrome has been selected for the FDA's START Program, which aims to accelerate the development of rare disease therapeutics. This inclusion could expedite the therapy's path to market, potentially boosting Neurogene's stock.
The inclusion in the FDA's START Program is a significant milestone for Neurogene, as it provides enhanced communication with the FDA and could accelerate the development and approval process for NGN-401. This positive regulatory development is likely to boost investor confidence and positively impact the stock price in the short term.
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