FDA Grants RMAT Status to UniQure's AMT-130 Gene Therapy for Huntington's Disease
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The FDA has granted Regenerative Medicine Advanced Therapy (RMAT) designation to uniQure's AMT-130 gene therapy for Huntington's disease, based on promising interim Phase I/II clinical data.
June 03, 2024 | 11:17 am
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uniQure's AMT-130 gene therapy for Huntington's disease has received RMAT designation from the FDA, indicating strong potential to address a significant unmet medical need.
The RMAT designation from the FDA is a significant regulatory milestone that can expedite the development and review process of AMT-130. This recognition is based on promising interim Phase I/II clinical data, which suggests that the therapy has the potential to address a major unmet medical need in Huntington's disease. This news is likely to positively impact uniQure's stock price in the short term.
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