Mirum Pharmaceuticals Announces Phase 3 RESTORE Study Results Evaluating Chenodal In Patients With Cerebrotendinous Xanthomatosis
Portfolio Pulse from Benzinga Newsdesk
Mirum Pharmaceuticals, Inc. (NASDAQ:MIRM) has announced positive data from the Phase 3 RESTORE study evaluating Chenodal tablets in patients with cerebrotendinous xanthomatosis (CTX). The study met its primary endpoint with a significant reduction in bile alcohols. The company plans to submit these data to the FDA and file a new drug application in the first half of 2024.
October 02, 2023 | 12:33 pm
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Positive results from Mirum Pharmaceuticals' Phase 3 RESTORE study could boost investor confidence and potentially lead to an increase in the company's stock price.
The positive results from the Phase 3 RESTORE study are a significant milestone for Mirum Pharmaceuticals. This could lead to increased investor confidence in the company's ability to bring Chenodal to market, potentially leading to an increase in the company's stock price. The company's plan to file a new drug application with the FDA in the first half of 2024 also provides a clear timeline for potential regulatory approval, which could further boost investor confidence.
CONFIDENCE 90
IMPORTANCE 80
RELEVANCE 100